Waking up the silenced beauty: CRISPR/Cas9 mediated reactivation of fetal hemoglobin genes to treat severe beta-thalassemia in young patients.

Life Med

Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology and School of Life Sciences, East China Normal University, Shanghai 200241, China.

Published: April 2023

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Source
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC11749768PMC
http://dx.doi.org/10.1093/lifemedi/lnad009DOI Listing

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