Gene editing efficiencies and hematopoietic stem cell fitness in sickle cell disease: A balancing act.

Mol Ther

Department of Women and Children's Health, School of Life Course Sciences, Faculty of Life Sciences & Medicine, King's College London, London, UK; Harris Birthright Research Centre for Foetal Medicine, King's College Hospital, London SE5 8BB, UK; Peter Gorer Department of Immunobiology, School of Immunology & Microbial Sciences, Faculty of Life Sciences & Medicine, King's College London, London, UK.

Published: December 2024

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Source
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC11638869PMC
http://dx.doi.org/10.1016/j.ymthe.2024.11.009DOI Listing

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