Weighing the Risks of Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy.

N Engl J Med

From the Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland.

Published: October 2024

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http://dx.doi.org/10.1056/NEJMe2409399DOI Listing

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