Advanced gene and cellular therapies risk a second "valley of death" due to their high costs and low patient population. As these are life-saving therapies, measures are urgently needed to prevent their withdrawal from the market.

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http://www.ncbi.nlm.nih.gov/pmc/articles/PMC9900339PMC
http://dx.doi.org/10.15252/embr.202256661DOI Listing

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