AI Article Synopsis

  • Inborn errors of immunity (IEI) are genetic disorders affecting the immune system, and Next-Generation Sequencing (NGS) is key for their diagnosis.
  • A study in Chandigarh, North India, highlights the successful establishment of NGS facilities over three years, utilizing a custom gene panel to identify pathogenic variants in 121 IEI patients.
  • The results indicated that 77 patients had identifiable genetic mutations linked to various immune deficiencies, enhancing their access to genetic counseling, prenatal diagnosis, and treatment options.

Article Abstract

Inborn errors of immunity (IEI) are a heterogeneous group of monogenic disorders that include primary immunodeficiency's and other disorders affecting different aspects of the immune system. Next-Generation Sequencing (NGS) is an essential tool to diagnose IEI. We report our 3-year experience in setting up facilities for NGS for diagnosis of IEI in Chandigarh, North India. We used a targeted, customized gene panel of 44 genes known to result in IEI. Variant analysis was done using Ion Reporter software. The in-house NGS has enabled us to offer genetic diagnoses to patients with IEI at minimal costs. Of 121 patients who were included pathogenic variants were identified in 77 patients. These included patients with Chronic Granulomatous Disease, Severe Combined Immune Deficiency, leukocyte adhesion defect, X-linked agammaglobulinemia, Ataxia Telangiectasia, Hyper-IgE syndrome, Wiskott Aldrich syndrome, Mendelian susceptibility to mycobacterial diseases, Hyper-IgM syndrome, autoimmune lymphoproliferative syndrome, and GATA-2 deficiency. This manuscript discusses the challenges encountered while setting up and running targeted NGS for IEI in our unit. Genetic diagnosis has helped our patients with IEI in genetic counselling, prenatal diagnosis, and accessing appropriate therapeutic options.

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Source
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC9213413PMC
http://dx.doi.org/10.1038/s41598-022-14522-1DOI Listing

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