Ciliary Dyneins and Dynein Related Ciliopathies.

Cells

Center for Pediatrics and Adolescent Medicine, University Hospital Freiburg, Freiburg University Faculty of Medicine, Mathildenstrasse 1, 79106 Freiburg, Germany.

Published: July 2021

AI Article Synopsis

  • Cilia are crucial for vertebrate development and health, but their importance has often been overlooked.
  • Ciliopathies, a group of disorders caused by ciliary dysfunction, are primarily linked to issues with dynein motor activity affecting ciliary transport and movement.
  • The review discusses the different roles of cytoplasmic dynein-2 and axonemal dynein, highlighting the severe conditions linked to each type, and offers insights into their mechanisms and recent advancements in research.

Article Abstract

Although ubiquitously present, the relevance of cilia for vertebrate development and health has long been underrated. However, the aberration or dysfunction of ciliary structures or components results in a large heterogeneous group of disorders in mammals, termed ciliopathies. The majority of human ciliopathy cases are caused by malfunction of the ciliary dynein motor activity, powering retrograde intraflagellar transport (enabled by the cytoplasmic dynein-2 complex) or axonemal movement (axonemal dynein complexes). Despite a partially shared evolutionary developmental path and shared ciliary localization, the cytoplasmic dynein-2 and axonemal dynein functions are markedly different: while cytoplasmic dynein-2 complex dysfunction results in an ultra-rare syndromal skeleto-renal phenotype with a high lethality, axonemal dynein dysfunction is associated with a motile cilia dysfunction disorder, primary ciliary dyskinesia (PCD) or Kartagener syndrome, causing recurrent airway infection, degenerative lung disease, laterality defects, and infertility. In this review, we provide an overview of ciliary dynein complex compositions, their functions, clinical disease hallmarks of ciliary dynein disorders, presumed underlying pathomechanisms, and novel developments in the field.

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Source
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8391580PMC
http://dx.doi.org/10.3390/cells10081885DOI Listing

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