A panel of experts representing academic centers, family foundations and pharmaceutical industry came together to formulate a treatment algorithm for infants diagnosed via newborn screening (NBS) with Spinal muscular atrophy (SMA).
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| http://www.ncbi.nlm.nih.gov/pmc/articles/PMC6942550 | PMC |
| http://dx.doi.org/10.15844/pedneurbriefs-33-5 | DOI Listing |
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