A Matter of Genes: The Hurdles of Gene Therapy for Epilepsy.

Epilepsy Curr

1 Department of Medical Sciences and National Institute of Neuroscience, University of Ferrara, Ferrara, Italy.

Published: January 2019

Gene therapy has recently advanced to the level of standard of care for several diseases. However, its application to neurological disorders is still in the experimental phase. In this review, we discuss recent advancements in the field that provide optimism on the possibility to have first-in-human studies for gene therapy of some forms of epilepsy in the not so distant future.

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http://www.ncbi.nlm.nih.gov/pmc/articles/PMC6610370PMC
http://dx.doi.org/10.1177/1535759718822846DOI Listing

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