In this issue of Antoniani et al identify an innovative genome editing approach to induce fetal hemoglobin (HbF), which may eventually lead to therapeutic strategies for ameliorating or curing sickle-cell disease (SCD) and β-thalassemia.
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| http://www.ncbi.nlm.nih.gov/pmc/articles/PMC5921966 | PMC |
| http://dx.doi.org/10.1182/blood-2018-03-839787 | DOI Listing |
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