Safety of rAAV2/2-ND4 Gene Therapy for Leber Hereditary Optic Neuropathy.

Catherine Vignal Scott Uretsky Serge Fitoussi Anne Galy Laure Blouin Jean-François Girmens Samuel Bidot Nitza Thomasson Céline Bouquet Sonia Valero Sandrine Meunier Jean-Philippe Combal Bernard Gilly Barrett Katz José-Alain Sahel

Ophthalmology

Centre d'Investigation Clinique 1423, Inserm-DGOS, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France; Rothschild Ophthalmology Foundation Hospital, Paris, France; Sorbonne Université, INSERM, CNRS, Institut de la Vision, Paris, France; Department of Ophthalmology, University of Pittsburgh School of Medicine, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania.

Published: June 2018

Download full-text PDF	Source
http://dx.doi.org/10.1016/j.ophtha.2017.12.036	DOI Listing

Publication Analysis

Top Keywords

safety raav2/2-nd4

raav2/2-nd4 gene

gene therapy

therapy leber

leber hereditary

hereditary optic

optic neuropathy

safety

gene

therapy

Similar Publications

Want AI Summaries of new PubMed Abstracts delivered to your In-box?

Enter search terms and have AI summaries delivered each week - change queries or unsubscribe any time!