AI Article Synopsis
- The study suggests that hematopoietic cell transplantation (HCT) performed before the appearance of neurological symptoms in children with OSTM1 osteopetrosis is ineffective in stopping the progression of neurological issues.
- This indicates that the timing of HCT may not significantly alter the course of neurological deterioration in these patients.
- Further research may be needed to explore alternative treatments or interventions to address neurological symptoms associated with OSTM1 osteopetrosis.
Article Abstract
HCT prior to onset of neurologic symptoms in children with OSTM1 osteopetrosis does not halt neurologic progression.
Download full-text PDF |
Source |
|---|---|
| http://www.ncbi.nlm.nih.gov/pmc/articles/PMC5727773 | PMC |
| http://dx.doi.org/10.1182/bloodadvances.2016002345 | DOI Listing |
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