Experience of gastrostomy using a quality care framework: the example of rett syndrome.

Medicine (Baltimore)

From the Telethon Kids Institute (JD, KW, PJ, HL), The University of Western Australia; School of Physiotherapy and Exercise Science (JD), Curtin University, Perth, Australia; Department of Gastroenterology (MR), Princess Margaret Hospital, Perth, Australia; Discipline of Genetic Medicine (CE, JC); Discipline of Paediatrics and Child Health (CE, EJE, JC), The University of Sydney, The Children's Hospital at Westmead; and The Sydney Children's Hospitals Network (Westmead) (CE, EJE, JC), Sydney, Australia.

Published: December 2014

Rett syndrome is one of many severe neurodevelopmental disorders with feeding difficulties. In this study, associations between feeding difficulties, age, MECP2 genotype, and utilization of gastrostomy were investigated. Weight change and family satisfaction following gastrostomy were explored. Data from the longitudinal Australian Rett Syndrome Database whose parents provided data in the 2011 family questionnaire (n=229) were interrogated. We used logistic regression to model relationships between feeding difficulties, age group, and genotype. Content analysis was used to analyze data on satisfaction following gastrostomy. In those who had never had gastrostomy and who fed orally (n=166/229), parents of girls<7 years were more concerned about food intake compared with their adult peers (odds ratio [OR] 4.26; 95% confidence interval [CI] 1.29, 14.10). Those with a p.Arg168 mutation were often perceived as eating poorly with nearly a 6-fold increased odds of choking compared to the p.Arg133Cys mutation (OR 5.88; 95% CI 1.27, 27.24). Coughing, choking, or gagging during meals was associated with increased likelihood of later gastrostomy. Sixty-six females (28.8%) had a gastrostomy, and in those, large MECP2 deletions and p.Arg168 mutations were common. Weight-for-age z-scores increased by 0.86 (95% CI 0.41, 1.31) approximately 2 years after surgery. Families were satisfied with gastrostomy and felt less anxious about the care of their child. Mutation type provided some explanation for feeding difficulties. Gastrostomy assisted the management of feeding difficulties and poor weight gain, and was acceptable to families. Our findings are likely applicable to the broader community of children with severe disability.

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http://www.ncbi.nlm.nih.gov/pmc/articles/PMC4603139PMC
http://dx.doi.org/10.1097/MD.0000000000000328DOI Listing

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