Publications by authors named "Tay Salimullah"
Orphanet J Rare Dis
February 2024
Article Synopsis
- Health technology assessment (HTA) for pharmaceuticals, especially rare disease treatments, involves complexities and uncertainties due to faster approval processes.
- Real-world evidence (RWE) is being proposed to support HTA decisions, but its collection and application come with significant methodological challenges.
- The paper emphasizes the importance of rigorous study design and analysis in using RWE, and offers suggestions to enhance its effectiveness in HTA, highlighting its growing role in determining coverage and pricing.
