Publications by authors named "Sarah R Rivera"
Article Synopsis
- Duchenne muscular dystrophy (DMD) is a serious childhood condition with limited lifetime expectations, and current care guidelines lack updates on new medications and steroid dosing.
- A systematic review and expert feedback were used to create a list of recommendations for DMD therapies, employing a modified Delphi method to gather panelist insights.
- Preferred treatments include deflazacort or weekend dosing of prednisone, and patients with specific mutations should be considered for eteplirsen alongside corticosteroids, highlighting the need to weigh benefits against potential side effects in treatment choices.
