Publications by authors named "Kate Illei"
J Neuromuscul Dis
May 2023
Article Synopsis
- Duchenne muscular dystrophy (DMD) shows significant variability in how fast it progresses and how well patients respond to treatments, complicating the development of new therapies.
- A study analyzed data from boys with DMD to test if early clinical measures could predict different rates of disease progression.
- Results identified three distinct progression classes, revealing that early steroid treatment led to better motor function, and specific gene mutations were linked to slower disease progression.
