The use of rapamycin to treat vascular tumours and malformations: A single-centre experience.

Objectives: To assess the safety and efficacy of rapamycin in treating children with vascular tumours and malformations.

Study Design: We performed a retrospective review at a large tertiary care paediatric centre to assess the efficacy and safety of using rapamycin to treat vascular tumours and malformations. Response to therapy was defined by patient-reported symptom improvement, radiological reduction in size of lesions, and/or improvement of laboratory parameters.