Publications by authors named "Anna Moreno Garcia"
Mol Ther Nucleic Acids
September 2024
Article Synopsis
- - Recombinant adeno-associated virus (rAAV) gene therapies have great potential for treating various genetic disorders, requiring ongoing innovation in their development.
- - The novel miQURE technology utilizes microRNAs to target and silence toxic genes, and has evolved into the linQURE platform, which allows for simultaneous control of multiple gene expressions.
- - By demonstrating the capability to express two synthetic miRNAs together, linQURE enhances the effectiveness of gene therapy for complex diseases with multiple genetic contributors, ultimately broadening treatment options.
