Publications by authors named "Alexander F F J E Vrancken"
Drug treatment for spinal muscular atrophy type I.
Renske I Wadman Wendy M J Bosboom W Ludo van der Pol Leonard H van den Berg John H J Wokke Alexander F F J E Vrancken
Cochrane Database Syst Rev
April 2012
Background: Spinal muscular atrophy (SMA) is caused by degeneration of anterior horn cells of the spinal cord, which leads to progressive muscle weakness. Children with SMA type I will never be able to sit without support and usually die by the age of two years. There are no known efficacious drug treatments that influence the course of the disease.
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